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Genetics
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Niagen Bioscience Announces First-Ever Peer-Reviewed Study Highlighting the Potential of Nicotinamide Riboside (NR) for Werner Syndrome, a Rare Genetic Disorder

LOS ANGELES--(BUSINESS WIRE)--Niagen Bioscience, Inc. (NASDAQ: NAGE) (formerly ChromaDex Corp.), the global authority on NAD+ (nicotinamide adenine dinucleotide) with a focus on the science of healthy aging, shares positive results from a clinical study published in the peer-reviewed journal Aging Cell, by a team led by Masaya Koshizaka, M.D., Ph.D., Associate Professor, and Koutaro Yokote, M.D., Ph.D., MBA, President of Chiba University, both of the Center for Preventive Medical Sciences, Chib...
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Samenvatting: Alnylam krijgt goedkeuring van Europese Commissie voor AMVUTTRA® (vutrisiran) voor de behandeling van ATTR amyloïdose met cardiomyopathie

CAMBRIDGE, Mass.--(BUSINESS WIRE)--Alnylam Pharmaceuticals, Inc. (Nasdaq: ALNY), het toonaangevende bedrijf op het gebied van RNA-interferentietherapie (RNAi), kondigde vandaag aan dat de Europese Commissie (EC) een goedkeuring heeft verleend voor de behandeling van wildtype of erfelijke transthyretine amyloïdose bij volwassen patiënten met cardiomyopathie (ATTR-CM) als een aanvullende indicatie voor zijn RNAi-weestherapie AMVUTTRA® (vutrisiran). Deze bekendmaking is officieel geldend in de ori...
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Cure Rare Disease Welcomes New Scientific and Strategic Leaders to Advance Therapies for Ultra-Rare Conditions

WOODBRIDGE, Conn.--(BUSINESS WIRE)--Cure Rare Disease (CRD), a clinical-stage nonprofit biotechnology organization developing genetic therapies for ultra-rare conditions, is proud to announce the appointment of Keith Sutton, PhD, as Chief Science Officer and the addition of Michelle Werner to its Board of Directors. These strategic additions bring deep scientific expertise and seasoned biopharmaceutical leadership to CRD as the organization continues to advance therapeutic development for rare...
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All in for CTF: Jason Colodne and Colbeck Capital Support Children’s Tumor Foundation Charity Poker Tournament

NEW YORK--(BUSINESS WIRE)--Colbeck Capital Management, a leading middle-market private credit firm focused on strategic lending, today announced its continued support of the Children’s Tumor Foundation (“CTF” or the “Foundation”) through sponsorship of its 2025 New York City Charity Poker Tournament. The tournament, to be held June 12 at The Prince George Ballroom, invites participants to “go all in” for the Children’s Tumor Foundation and features a cocktail reception followed by Texas Hold ‘E...
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CGT Global Supports Renown Health in Advancing Breast Cancer Treatment in Nevada

RENO, Nev.--(BUSINESS WIRE)--CGT Global supports Renown Health’s new Conrad Breast Center, expanding access to life-changing cancer care in Nevada....
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Taconic Biosciences Enters Into an Exclusive License Agreement With Helmholtz Munich to Expand Its CRISPR/Cas9 Gene Editing Services

RENSSELAER, N.Y.--(BUSINESS WIRE)--Taconic Biosciences has acquired the exclusive rights to a patented CRISPR-based gene editing technology for biomedical research....
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Alnylam Receives European Commission Approval for AMVUTTRA® (vutrisiran) for the Treatment of ATTR Amyloidosis with Cardiomyopathy

CAMBRIDGE, Mass.--(BUSINESS WIRE)--Alnylam Pharmaceuticals, Inc. (Nasdaq: ALNY), the leading RNA interference (RNAi) therapeutics company, today announced that the European Commission (EC) has granted approval for the treatment of wild-type or hereditary transthyretin amyloidosis in adult patients with cardiomyopathy (ATTR-CM) as an additional indication for its orphan RNAi therapeutic AMVUTTRA® (vutrisiran). The approval broadens the indication for AMVUTTRA, which now becomes the first and onl...
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SOLVE FSHD and Modalis Announce Strategic Collaboration to Develop an Innovative CRISPR-Based Epigenome Editing Treatment for Facioscapulohumeral Muscular Dystrophy

VANCOUVER, British Columbia & TOKYO & WALTHAM, Mass.--(BUSINESS WIRE)--SOLVE FSHD and Modalis partner to develop a CRISPR-based epigenome editing therapy for facioscapulohumeral muscular dystrophy (FSHD)....
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Neurogene Announces Inducement Grants Under Nasdaq Listing Rule 5635(c)(4)

NEW YORK--(BUSINESS WIRE)--Neurogene Inc. (Nasdaq: NGNE), a clinical-stage company founded to bring life-changing genetic medicines to patients and families affected by rare neurological diseases, today announced that the Compensation Committee of the Company’s Board of Directors approved the grant of non-qualified stock options to purchase an aggregate of 39,345 shares of the Company’s common stock to four new employees (the “Inducement Grants”) on June 5, 2025 (the “Grant Date”). The Induceme...
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Riassunto: Biocytogen ottiene il brevetto giapponese per la piattaforma RenMab, ampliando il proprio portafoglio di brevetti globali per la piattaforma RenMice di anticorpi/TCR completamente umani

PECHINO--(BUSINESS WIRE)--Biocytogen Pharmaceuticals (Beijing) Co., Ltd. (Biocytogen, HKEX: 02315) ha annunciato oggi che la tecnologia chiave della sua piattaforma RenMab™ di topi con anticorpi completamente umani sviluppata in modo indipendente ha ottenuto un brevetto di invenzione dall'Ufficio Brevetti Giapponese. Questo traguardo segna un passo significativo nel rafforzamento del portafoglio di proprietà intellettuale globale della famiglia di piattaforme di anticorpi completamente umani Re...